Project: Development of the first pharmaceutical therapy for the Allan-Herndon-Dudley Syndrome (AHDS)

Acronym TREAT-AHDS (Reference Number: 11337)
Duration 01/09/2017
Project Topic The consortium will develop the first pharmaceutical treatment for AHDS, a rare type of X-linked mental retardation associated with physical disability and premature death. The project will advance this orphan drug towards marketing approval by conducting a Phase IIb clinical trial in young AHDS children, improving development of diagnostic and monitoring methods relating to the condition, optimize the formulation, interact with key regulatory agencies and develop the relevant documentation.
Network Eurostars 2
Call Eurostars Cut-Off 7

Project partner

Number Name Role Country
1 Medical Need Europe AB Coordinator Sweden
2 Erasmus Medical Center Partner Netherlands